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Safety, tolerability, and efficacy of subcutaneous efgartigimod in patients with chronic inflammatory demyelinating polyradiculoneuropathy (ADHERE): a multicentre, randomised-withdrawal, double-blind, placebo-controlled, phase 2 trial

Jeffrey A. Allen, Jie Lin, Ivana Basta, Tina Dysgaard, Christian Eggers, Jeffrey T. Guptill, Kelly Gwathmey, Channa Hewamadduma, Erik Hofman, Yessar Hussain, Satoshi Kuwabara, Gwendal Le Masson, Frank Leypoldt, Ting Chang, Marta Lipowska, Murray Lowe, Giuseppe Lauria, Luís Querol, Mihaela-Adriana Simu, Niraja Suresh, Anissa Tse, Peter Ulrichts, Benjamin Van Hoorick, Ryo Yamasaki, Richard A. Lewis, Pieter A. van Doorn, Susanne Grinzinger, Julia Wanschitz, Thomas Seifert-Held, Kristl G. Claeys, Jonathan Baets, Gauthier Remiche, Véronique Bissay, Nicolas Dubuisson, Stephanie Delstanche, Ivaylo Tarnev, Krasimir Genov, Plamen Tsvetanov, Ivan Milanov, Chongbo Zhao, Bitao Bu, Xuefan Yu, Wei Li, Haishan Jiang, Yuwei Da, Zuneng Lu, Hui Liang, Fuqiang Guo, Zunbo Li, Zhangyu Zou, Daojun Hong, Huan Yang, Junhong Guo, Jianquan Shi, Jianglong Tu, Dian He, Yiqi Wang, Jing Ding, Yali Zhang, Yuanqi Zhao, Renxi Xu, Yunhua Yue, Aihong Guo, Yuzhong Wang, Radomir Talab, Thomas Harbo, Soeren Sindrup, Jérôme De Seze, Sabrina Sacconi, Yann Péréon, Andoni Echaniz-Laguna, Laurent Magy, Guillaume Nicolas, Frédéric Taithe, Julien Cassereau, Rabab Debs, Roman Shakarishvili, Alexander Tsiskaridze, Maka Mania, Marina Janelidze, Tamar Janelidze, Michael Schroeter, Thomas Skripuletz, De-Hyung Lee, Juliane Klehmet, Benjamin Hotter, Olaf Hoffmann, Petra Baum, Jana Zschuentzsch, Kalliopi Pitarokoili, Mark Stettner, Dániel Bereczki, Gyula Pánczél, Alon Abraham, Amir Dori, Yair Lampl, Fiore Manganelli, Stefania Morino, Alessandro Padovani, Gabriele Siciliano

2024The Lancet Neurology96 citationsDOIOpen Access PDF

Topics & Concepts

MedicineTolerabilityPolyradiculoneuropathyWeaknessPlaceboMultifocal motor neuropathyInternal medicineAdverse effectImmunologySurgeryPathologyGuillain-Barre syndromeMismatch negativityElectroencephalographyPsychiatryAlternative medicinePeripheral Neuropathies and DisordersMyasthenia Gravis and ThymomaPeripheral Nerve Disorders
Safety, tolerability, and efficacy of subcutaneous efgartigimod in patients with chronic inflammatory demyelinating polyradiculoneuropathy (ADHERE): a multicentre, randomised-withdrawal, double-blind, placebo-controlled, phase 2 trial | Litcius