CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease phenotypes in a kidney organoid model

Sheng Cui, Yoo Jin Shin, Xianying Fang, Hanbi Lee, Sang Hun Eum, Eun Jeong Ko, Sun Woo Lim, Eun-Ji Shin, Kang In Lee, Jae Young Lee, Chae Bin Lee, Soo Kyung Bae, Chul Woo Yang, Byung Ha Chung