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Eliminating Panglossian thinking in development of AAV therapeutics

Radosław Kaczmarek, Glenn F. Pierce, Declan Noone, Brian O’Mahony, David Page, Mark W. Skinner

2021Molecular Therapy15 citationsDOIOpen Access PDF

Topics & Concepts

Food and drug administrationAdvisory committeeVector (molecular biology)Genetic enhancementMedicineToxicityGene transferGenomeGeneVirologyBiotechnologyBiologyPharmacologyPolitical scienceGeneticsInternal medicineRecombinant DNAPublic administrationVirus-based gene therapy researchCAR-T cell therapy researchViral Infectious Diseases and Gene Expression in Insects
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