AAV6 vectors provide superior gene transfer compared to AAV9 vectors following intramyocardial administration
Jianan Wang, Timo Jonker, Aina Cervera-Barea, Zhenyu Dong, R. Visser, Evelien Birza, Arnie Boender, Mischa Klerk, Yuting Yang, Joyce Visser, Marlijn Jansen, Tom C Grootswagers, Cindy I. Bart, Saskia C.A. de Jager, Silke Schrödel, Christian Thirion, osne kirzner, Hanno L. Tan, Antoine A.F. de Vries, Joost P. G. Sluijter, Klaus Neef, Joris R. de Groot, Vincent M. Christoffels, Gerard J.J. Boink
Abstract
assays, thereby facilitating the development of more potent AAV variants for cardio-selective delivery methods.
Topics & Concepts
Gene transferAdministration (probate law)BiologyMedicineGeneGeneticsPolitical scienceLawVirus-based gene therapy researchViral Infections and Immunology ResearchCRISPR and Genetic Engineering