Litcius/Paper detail

New approaches to moderate CRISPR-Cas9 activity: Addressing issues of cellular uptake and endosomal escape

Maja van Hees, Sofie Slott, Anders Højgaard Hansen, Heon Seok Kim, Hanlee P. Ji, Kira Astakhova

2021Molecular Therapy34 citationsDOIOpen Access PDF

Topics & Concepts

CRISPREndosomeBiologyCas9Genome editingComputational biologyCell biologyGeneticsGeneCellCRISPR and Genetic EngineeringRetinal Development and DisordersGenetics, Aging, and Longevity in Model Organisms