Litcius/Paper detail

Toxicity after AAV delivery of RNAi expression constructs into nonhuman primate brain

Megan S. Keiser, Paul T. Ranum, Carolyn M. Yrigollen, Ellie M. Carrell, Geary R. Smith, Amy Muehlmatt, Yong Hong Chen, Joel M. Stein, Ronald L. Wolf, Enrico Radaelli, Timothy Lucas, Pedro Gonzalez‐Alegre, Beverly L. Davidson

2021Nature Medicine73 citationsDOIOpen Access PDF

Topics & Concepts

RNA interferenceDicermicroRNABiologySpinocerebellar ataxiaRNAAdeno-associated virusAtaxiaContext (archaeology)NeuroscienceBioinformaticsGeneticsVector (molecular biology)GeneRecombinant DNAPaleontologyRNA Interference and Gene DeliveryRNA regulation and diseaseRNA Research and Splicing