Litcius/Paper detail

A Phase 2, Double-Blind, Randomized, Dose-Ranging Trial Of <i>Reldesemtiv</i> In Patients With ALS

Jeremy M. Shefner, Jinsy Andrews, Angela Genge, Carlayne E. Jackson, Noah Lechtzin, Timothy M. Miller, Bettina M. Cockroft, Lisa Meng, Jenny Wei, Andrew A. Wolff, Fady I. Malik, Cynthia Bodkin, Benjamin Rix Brooks, James B. Caress, Annie Dionne, Dominic B. Fee, Stephen A. Goutman, Namita Goyal, Orla Hardiman, Ghazala Hayat, Terry Heiman‐Patterson, Daragh Heitzman, Robert D. Henderson, Wendy Johnston, Chafic Karam, Matthew C. Kiernan, Stephen J. Kolb, Lawrence Korngut, Shafeeq Ladha, Geneviève Matte, Jesús S. Mora, Merrilee Needham, Björn Oskarsson, Gary L. Pattee, Erik P. Pioro, Michael Pulley, Dianna Quan, Kourosh Rezania, Kerri Schellenberg, David Schultz, Christen Shoesmith, Zachary Simmons, Jeffrey Statland, Shumaila Sultan, Andrea Swenson, Leonard H. van den Berg, Tuan Vu, Steve Vucic, Michael D. Weiss, Ashley Whyte-Rayson, James Wymer, Lorne Zinman, Stacy A. Rudnicki

2020Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration56 citationsDOIOpen Access PDF

Abstract

OBJECTIVE: on patients with ALS should be assessed in a pivotal Phase 3 trial. (ClinicalTrials.gov Identifier: NCT03160898).

Topics & Concepts

MedicinePlaceboInternal medicineTolerabilityStatistical significanceClinical endpointNauseaDiscontinuationAdverse effectRenal functionDose-ranging studyAmyotrophic lateral sclerosisRandomized controlled trialDouble blindDiseasePathologyAlternative medicineAmyotrophic Lateral Sclerosis ResearchCholinesterase and Neurodegenerative DiseasesNeurogenetic and Muscular Disorders Research