Body composition and weight changes after ivacaftor treatment in adults with cystic fibrosis carrying the G551 D cystic fibrosis transmembrane conductance regulator mutation: A double-blind, placebo-controlled, randomized, crossover study with open-label extension
Susannah J. King, Audrey Tierney, Deirdre Edgeworth, D. Keating, E. Williams, Tom Kotsimbos, Brenda Button, John Wilson
Topics & Concepts
IvacaftorCystic fibrosisBody mass indexCrossover studyPlaceboGastroenterologyInternal medicineMedicineCystic fibrosis transmembrane conductance regulatorEndocrinologyWeight gainAnimal scienceChemistryBody weightPathologyBiologyAlternative medicineCystic Fibrosis Research AdvancesAsthma and respiratory diseasesDelphi Technique in Research