Ambroxol increases glucocerebrosidase (GCase) activity and restores GCase translocation in primary patient-derived macrophages in Gaucher disease and Parkinsonism
Alena E. Kopytova, Georgy N. Rychkov, Михаил Николаев, Galina Baydakova, Alexander A. Cheblokov, Konstantin Senkevich, Darya Bogdanova, Olga I. Bolshakova, Irina Miliukhina, Vadim Bezrukikh, Galina Salogub, С. В. Саранцева, T.C. Usenko, Ekaterina Zakharova, Anton Emelyanov, С. Н. Пчелина
Topics & Concepts
GlucocerebrosidaseAmbroxolChemistryPeripheral blood mononuclear cellEnzymePharmacologyMolecular biologyImmunologyInternal medicineBiochemistryMedicineBiologyIn vitroAnesthesiaLysosomal Storage Disorders ResearchCellular transport and secretionCarbohydrate Chemistry and Synthesis