Litcius/Paper detail

First trial of ‘base editing’ in humans lowers cholesterol — but raises safety concerns

Miryam Naddaf

2023Nature33 citationsDOI

Topics & Concepts

Genome editingCholesterolGeneComputational biologyBiologyComputer scienceBioinformaticsGeneticsCRISPRBiochemistryCRISPR and Genetic EngineeringViral Infections and Immunology ResearchVirus-based gene therapy research