Litcius/Paper detail

Safety and efficacy of tamoxifen in boys with Duchenne muscular dystrophy (TAMDMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Bettina Henzi, Simone Schmidt, Sara Nagy, Daniela Rubino-Nacht, Sabine Schaedelin, Niveditha Putananickal, Georgia Stimpson, Deborah Ridout, Francesco Muntoni, Adnan Manzur, Rosaline C. M. Quinlivan, Giovanni Baranello, Marion Main, Lianne Abbott, N. Burnett, A. Rohwer, Evelin Milev, A. Wolfe, Emer O’Reilly, Volker Straub, Michela Guglieri, C. Marini Bettolo, Robert Muni‐Lofra, M. James, Jassi Sodhi, Tracey Willis, E. M. Wright, Claire Rylance, Nicola Birchall, Anne‐Marie Childs, Karen Pysden, Cristina Martos-Lozano, Lindsey Pallant, S. Wadsworth, Stefan Spinty, R Madhu, Rajesh Karuvattil, Sarah Gregson, Stuart Clark, Elizabeth Wraige, Heinz Jungbluth, Vasantha Gowda, Maria Vanegas, E Sheehan, Amy Wolfe, Alex Schofield, Imelda Hughes, Gary McCullagh, Emily J. Whitehouse, Uma Varma, Sinead Warner, Emily Reading, L.C. Benson, Tracey Willis, Jenny Moustoukas, Kate Strachan, N. Emery, Min Ong, Mark Atherton, Sarah D’Urso, Kay White, Neil Hinde, Kate Skone, Silvia Sanchez Marco, Anurag Saxena, Frances Gibbon, J.M. TeWaterNaude, Hayley L. Belnoue-Davis, Laura Thompson, Anirban Majumdar, Archana Murugan, M. A. M. Lynch, Emily Milton, Iolanda Guarino, Richard Tomlinson, Heather Jarvis, Jane M. Berry, Lucy Wills, Claire Frimpong-Ansah, Jackie Watson, Gemma Robertson, Gavin Cobb, Julie Burslem, Iain Horrocks, Jarod Wong, Andreas Brunklaus, Marina DiMarco, Sarah M. Brown, Susanne Mckenzie, Krupa Torne, Rana Mohamed, Vel Velmurugan, Manish Prasad, Saam Sedehizadeh, Sarah Williamson, Paula Fenty, Christian DeGoede, Amy Parkes, Marjorie Illingworth, Neeraj Bhangu

2023The Lancet Neurology22 citationsDOIOpen Access PDF

Topics & Concepts

Duchenne muscular dystrophyPlaceboMedicineTamoxifenDouble blindMuscular dystrophyPhysical therapyPhysical medicine and rehabilitationInternal medicineAlternative medicineBreast cancerCancerPathologyMuscle Physiology and DisordersAdipose Tissue and MetabolismTelomeres, Telomerase, and Senescence