Fourth Boy Dies in Clinical Trial of Astellas' AT132
Alex Philippidis
Topics & Concepts
Genetic enhancementMedicineDuchenne muscular dystrophyAdeno-associated virusMuscular dystrophyClinical trialGene deliveryGeneBioinformaticsInternal medicineVector (molecular biology)GeneticsBiologyRecombinant DNAVirus-based gene therapy researchTissue Engineering and Regenerative MedicineNeurogenetic and Muscular Disorders Research