A Rare Kidney Disease To Cure Them All? Towards Mechanism-Based Therapies for Proteinopathies
Moran Dvela‐Levitt, Jillian L. Shaw, Anna Greka
Topics & Concepts
KidneyInduced pluripotent stem cellDiseaseMedicineKidney diseaseMUC1Mechanism (biology)PathogenesisBiologyCancer researchBioinformaticsPathologyGeneGeneticsInternal medicineMucinPhilosophyEmbryonic stem cellEpistemologyRenal Diseases and GlomerulopathiesBiomedical Research and PathophysiologyLysosomal Storage Disorders Research