Litcius/Paper detail

Gene therapy and other novel treatment approaches for Charcot-Marie-Tooth disease

Chiara Pisciotta, Davide Pareyson

2023Neuromuscular Disorders30 citationsDOI

Topics & Concepts

Genetic enhancementMyelinMedicineGene silencingRNA interferenceCancer researchBioinformaticsGeneBiologyGeneticsInternal medicineRNACentral nervous systemHereditary Neurological DisordersSignaling Pathways in DiseaseNeurological diseases and metabolism