CRISPR-Cas9 Gene Therapy for Duchenne Muscular Dystrophy
Cédric Happi Mbakam, Gabriel Lamothe, Guillaume Tremblay, Jacques P. Tremblay
Topics & Concepts
CRISPRGenome editingDuchenne muscular dystrophyCas9DystrophinComputational biologyGenetic enhancementBiologyGuide RNAMuscular dystrophyGeneGeneticsBioinformaticsMedicineCRISPR and Genetic EngineeringVirus-based gene therapy researchGenetics, Aging, and Longevity in Model Organisms