Preclinical studies of gene replacement therapy for CDKL5 deficiency disorder
Gregory Voronin, Jana Narasimhan, Jamila Gittens, Josephine Sheedy, Philip Lipari, Melinda Peters, Steven J. DeMarco, Liangxian Cao, Yakov Varganov, Min Jung Kim, Lisset Pear, Eman Fotouh, Supriya Sinha, Balmiki Ray, Michael C. Wu, Padmaja Yalamanchili, Christopher Southgate, Joseph Pick, Khalil Saadipour, Stephen P. Jung, J.M. Lee, Anna Mollin, Ellen Welch, Zhijian Wu, Marla Weetall
Topics & Concepts
Genetic enhancementMedicineGeneBiologyGeneticsBioinformaticsGenetics and Neurodevelopmental DisordersAutism Spectrum Disorder ResearchGenomic variations and chromosomal abnormalities