Regulatory news: Avalglucosidase alfa‐ngpt (Nexviazyme) for late‐onset Pompe disease—<scp>FDA</scp> approval summary
Ann R. Punnoose, Linda Jo Bone Jeng, Janet W. Maynard, The Review Team
Topics & Concepts
BiostatisticsFood and drug administrationMedicineClinical pharmacologyDrugPharmacologyPublic healthNursingLysosomal Storage Disorders ResearchCarbohydrate Chemistry and SynthesisChild Nutrition and Feeding Issues