Diamond-Blackfan anemia in adults: In pursuit of a common approach for a rare disease
Deena Iskander, Noémi Roy, Elspeth Payne, Emma Drašar, Kelly Hennessy, Yvonne Harrington, Chrysi Christodoulidou, Anastasios Karadimitris, Leisa Batkin, Josu de la Fuente
Topics & Concepts
Diamond–Blackfan anemiaDiseaseMedicineBone marrow failureRepertoireRare diseaseAnemiaPediatricsIntensive care medicineBioinformaticsGeneticsGenePathologyInternal medicineBiologyStem cellPhysicsRibosomeAcousticsRNAHaematopoiesisRNA modifications and cancerCancer-related gene regulationEpigenetics and DNA Methylation