Recommendations for a minimum data set for monitoring gene therapy in hemophilia: communication from the ISTH SSC Working Group on Gene Therapy
Wolfgang Miesbach, Barbara A. Konkle, Pratima Chowdary, Radosław Kaczmarek, Frank W.G. Leebeek, Johnny Mahlangu, Michael Makris, Steven W. Pipe, Alok Srivastava, Jan Voorberg, Glenn F. Pierce, Flora Peyvandi
Topics & Concepts
Minimum Data SetData collectionMedicineSet (abstract data type)Data setData miningComputer scienceArtificial intelligenceStatisticsMathematicsNursing homesProgramming languageNursingHemophilia Treatment and ResearchCAR-T cell therapy research