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Diamond-Blackfan anemia, the archetype of ribosomopathy: How distinct is it from the other constitutional ribosomopathies?

Lydie Da Costa, Narla Mohandas, Ludivine David-NGuyen, Jessica Platon, Isabelle Marié, Marie Françoise O'Donohue, Thierry Leblanc, Pierre‐Emmanuel Gleizes

2024Blood Cells Molecules and Diseases15 citationsDOIOpen Access PDF

Topics & Concepts

Diamond–Blackfan anemiaArchetypeAnemiaMedicineBiologyGeneticsPhilosophyInternal medicineTheologyRNARibosomeGeneBlood disorders and treatmentsRNA modifications and cancerCardiac Structural Anomalies and Repair