Litcius/Paper detail

Vosoritide therapy in children with achondroplasia aged 3−59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial

Ravi Savarirayan, William R. Wilcox, Paul Harmatz, John H. Phillips, Lynda E. Polgreen, Louise Tofts, Keiichi Ozono, Paul Arundel, Melita Irving, Carlos A. Bacino, Donald Basel, Michael B. Bober, Joel Charrow, Hiroshi Mochizuki, Yumiko Kotani, Howard M. Saal, Clare Army, George Jeha, Yulan Qi, Lynn Han, Elena Fisheleva, Alice Huntsman-Labed, Jonathan Day

2023The Lancet Child & Adolescent Health64 citationsDOI

Topics & Concepts

AchondroplasiaPlaceboMedicineDouble blindPhysical therapyPhase (matter)Multinational corporationPediatricsAlternative medicinePolitical scienceChemistryOrganic chemistryLawPathologyConnective tissue disorders researchInfant Nutrition and HealthDermatological and Skeletal Disorders