Vosoritide therapy in children with achondroplasia aged 3−59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial
Ravi Savarirayan, William R. Wilcox, Paul Harmatz, John H. Phillips, Lynda E. Polgreen, Louise Tofts, Keiichi Ozono, Paul Arundel, Melita Irving, Carlos A. Bacino, Donald Basel, Michael B. Bober, Joel Charrow, Hiroshi Mochizuki, Yumiko Kotani, Howard M. Saal, Clare Army, George Jeha, Yulan Qi, Lynn Han, Elena Fisheleva, Alice Huntsman-Labed, Jonathan Day
Topics & Concepts
AchondroplasiaPlaceboMedicineDouble blindPhysical therapyPhase (matter)Multinational corporationPediatricsAlternative medicinePolitical scienceChemistryOrganic chemistryLawPathologyConnective tissue disorders researchInfant Nutrition and HealthDermatological and Skeletal Disorders