A targeted approach: Gene and RNA editing for neurodegenerative disease treatment
Chen‐Wei Huang, Wen‐Gen Zhang, Yan Liao, Ting Hu, Jiamei Li, Changli Wang
Topics & Concepts
Genome editingComputational biologyDiseaseGeneRNA editingRNABiologyGeneticsBioinformaticsMedicineNeuroscienceCRISPRPathologyCRISPR and Genetic EngineeringRNA regulation and diseaseVirus-based gene therapy research