P.132 Casimersen in patients with Duchenne muscular dystrophy amenable to exon 45 skipping: Interim results from the Phase 3 ESSENCE trial
S. Iannaccone, H. Phan, V. Straub, F. Muntoni, D. Wolf, J. Malhotra, Ruzai Chu, E. Darton, E. Mercuri
Topics & Concepts
Duchenne muscular dystrophyInterimExon skippingMedicineInterim analysisPhase (matter)Physical medicine and rehabilitationExonClinical trialInternal medicineGeneticsBiologyPhysicsGenePolitical scienceAlternative splicingLawQuantum mechanicsMuscle Physiology and DisordersNeuroscience and Neural Engineering