Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial

Andreas Glenthøj, Eduard J. van Beers, Hanny Al‐Samkari, Vip Viprakasit, Kevin H.M. Kuo, Frederic Galactéros, Satheesh Chonat, John B. Porter, Erin Zagadailov, Rengyi Xu, Abdulafeez Oluyadi, Peter Hawkins, Sarah Gheuens, Vanessa Beynon, Wilma Barcellini