Whole-brain in vivo base editing reverses behavioral changes in Mef2c-mutant mice
Wei-Ke Li, Shu-Qian Zhang, Wanling Peng, Yuhan Shi, Bo Yuan, Yiting Yuan, Zhenyu Xue, Jincheng Wang, Wenjian Han, Zhifang Chen, Shifang Shan, Biqing Xue, Jinlong Chen, Cheng Zhang, Shujia Zhu, Yilin Tai, Tian‐Lin Cheng, Zilong Qiu
Topics & Concepts
MutantMutationBiologyGeneticsIn vivoGeneCRISPR and Genetic EngineeringRNA regulation and diseaseRNA and protein synthesis mechanisms