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The landscape of CRISPR/Cas9 for inborn errors of metabolism

Andrés Felipe Leal, Nidhi Fnu, Eliana Benincore-Flórez, Angelica María Herreño-Pachón, Olga Yaneth Echeverri-Peña, Carlos Javier Alméciga-Díaz, Shunji Tomatsu

2022Molecular Genetics and Metabolism22 citationsDOIOpen Access PDF

Topics & Concepts

CRISPRCas9Genome editingComputational biologyContext (archaeology)BiologyGeneGenomeGeneticsEpigeneticsPaleontologyCRISPR and Genetic EngineeringGenetics and Neurodevelopmental DisordersGenomics and Rare Diseases
The landscape of CRISPR/Cas9 for inborn errors of metabolism | Litcius