Safety and efficacy of losmapimod in facioscapulohumeral muscular dystrophy (ReDUX4): a randomised, double-blind, placebo-controlled phase 2b trial
Rabi Tawil, Kathryn R. Wagner, Johanna Hamel, Doris G. Leung, Jeffrey Statland, Leo H. Wang, Angela Genge, Sabrina Sacconi, Hanns Lochmüller, David Reyes‐Leiva, Jordi Díaz‐Manera, Jorge Alonso‐Pérez, Nuria Muelas, Juan J. Vílchez, Alan Pestronk, Summer Gibson, Namita Goyal, Lawrence J. Hayward, Nicholas J. Johnson, Samantha LoRusso, Miriam Freimer, Perry B. Shieh, S. H. Subramony, Baziel G.M. van Engelen, Joost Kools, Olof Dahlqvist Leinhard, Per Widholm, Christopher Morabito, Christopher M. Moxham, Diego Cadavid, Michelle Mellion, Adefowope Odueyungbo, William Tracewell, Anthony Accorsi, Lucienne Ronco, Robert J. Gould, Jennifer Shoskes, Luis Alejandro Rojas, John Jiang
Topics & Concepts
Facioscapulohumeral muscular dystrophyMedicineTolerabilityClinical endpointPlaceboMuscular dystrophyInternal medicinePhysical therapyClinical trialSurrogate endpointMuscle biopsyAdverse effectBiopsyPathologyAlternative medicineMuscle Physiology and DisordersCardiomyopathy and Myosin StudiesGenetic Neurodegenerative Diseases