CRISPR/Cas9 gene editing for curing sickle cell disease
So Hyun Park, Gang Bao
Topics & Concepts
Genome editingCRISPRMedicineDiseaseGenetic enhancementHematopoietic stem cell transplantationFetal hemoglobinHaematopoiesisStem cellCas9TransplantationEx vivoImmunologyBioinformaticsCancer researchGeneBiologyIn vivoFetusInternal medicineGeneticsPregnancyCRISPR and Genetic EngineeringHemoglobinopathies and Related DisordersMosquito-borne diseases and control