Development of new outcome measures for adult SMA type III and IV: a multimodal longitudinal study
Giorgia Querin, Timothée Lenglet, Rabab Debs, Tanya Stojkovic, Anthony Béhin, François Salachas, Nadine Le Forestier, Maria del Mar Amador, Gaëlle Bruneteau, Pascal Laforêt, Sophie Blancho, Véronique Marchand‐Pauvert, Peter Bede, Jean‐Yves Hogrel, Pierre-François Pradat
Topics & Concepts
MedicineSMA*Spinal muscular atrophyClinical trialPhysical medicine and rehabilitationSample size determinationMagnetic resonance imagingPhysical therapyInternal medicineRadiologyDiseaseCombinatoricsStatisticsMathematicsNeurogenetic and Muscular Disorders ResearchCardiomyopathy and Myosin StudiesMuscle activation and electromyography studies