RNA interference (RNAi)-based therapeutics for treatment of rare neurologic diseases
Noélle D. Germain, Wendy K. Chung, Patrick D. Sarmiere
Topics & Concepts
RNA interferenceSmall hairpin RNAComputational biologymicroRNABiologyOligonucleotideSmall interfering RNARNAGeneRNA silencingDiseaseGene silencingGenomeBioinformaticsGeneticsMedicinePathologyRNA regulation and diseaseNeurogenetic and Muscular Disorders ResearchCRISPR and Genetic Engineering