Litcius/Paper detail

First in vivo base-editing trial shows promise

Renzhi Han

2023Molecular Therapy12 citationsDOIOpen Access PDF

Topics & Concepts

CRISPRGenome editingCas9Genetic enhancementFood and drug administrationBiologyComputational biologyGeneMedicineGeneticsPharmacologyCRISPR and Genetic EngineeringInnovation and Socioeconomic DevelopmentGenetics, Aging, and Longevity in Model Organisms
First in vivo base-editing trial shows promise | Litcius