Ensuring a future for gene therapy for rare diseases
Alessandro Aiuti, Francesca Pasinelli, Luigi Naldini
Topics & Concepts
Genetic enhancementIntensive care medicineDiseaseMedicineHematopoietic stem cellHaematopoiesisStem cellGeneInternal medicineBiologyGeneticsImmunodeficiency and Autoimmune DisordersNeurogenetic and Muscular Disorders ResearchVirus-based gene therapy research