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Life-Saving, Dose-Adjusted, Targeted Therapy in a Patient with a STAT3 Gain-of-Function Mutation

Eytan Sarfati, Jérôme Hadjadj, Mathieu Fusaro, Roman Klifa, Marion Grimaud, Laureline Berteloot, Alice Hadchouel, Cécile Godot, Marie‐Claude Stolzenberg, Marie‐Louise Frémond, Claire Pressiat, Thierry Jo Molina, Alain Fischer, Capucine Pïcard, Sylvain Renolleau, Frédéric Rieux‐Laucat, Stéphane Blanche, Bénédicte Neven

2021Journal of Clinical Immunology21 citationsDOI

Topics & Concepts

Gain of functionMedical microbiologyMutationMedicineFunction (biology)OncologyInternal medicineIntensive care medicineGeneticsBiologyImmunologyGeneCytokine Signaling Pathways and InteractionsImmunodeficiency and Autoimmune DisordersLung Cancer Treatments and Mutations
Life-Saving, Dose-Adjusted, Targeted Therapy in a Patient with a STAT3 Gain-of-Function Mutation | Litcius