Litcius/Paper detail

Base editing: advances and therapeutic opportunities

Elizabeth M. Porto, Alexis C. Komor, Ian M. Slaymaker, G Yeo

2020Nature Reviews Drug Discovery472 citationsDOIOpen Access PDF

Topics & Concepts

Computational biologyGenome editingRNADNAPoint mutationPrecision medicineBiologyRNA editingGeneticsBase pairBase (topology)GenomeComputer scienceMutationGeneMathematicsMathematical analysisCRISPR and Genetic EngineeringVirus-based gene therapy researchRNA regulation and disease