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Disease mechanisms and gene therapy for Usher syndrome

Gwenaelle G.S. Géléoc, A. Amraoui

2020Hearing Research78 citationsDOIOpen Access PDF

Topics & Concepts

Usher syndromeBiologyRetinitis pigmentosaHearing lossPhenotypeGeneticsNeuroscienceMedicineGeneBioinformaticsAudiologyHearing, Cochlea, Tinnitus, GeneticsRetinal Development and DisordersRNA regulation and disease
Disease mechanisms and gene therapy for Usher syndrome | Litcius