Duchenne muscular dystrophy: Current treatment and emerging exon skipping and gene therapy approach
Grant Patterson, Haley Conner, Mecham Groneman, Cyril Blavo, Mayur Parmar
Topics & Concepts
Exon skippingDuchenne muscular dystrophyMedicineDystrophinWeaknessMuscular dystrophyBioinformaticsEnzyme replacement therapyDiseaseMyopathyGenetic enhancementExonIntensive care medicineInternal medicineSurgeryGeneticsBiologyGeneAlternative splicingMuscle Physiology and DisordersTissue Engineering and Regenerative MedicineCardiomyopathy and Myosin Studies