Genome sequencing and RNA sequencing of urinary cells reveal an intronic FBN1 variant causing aberrant splicing
Takuya Hiraide, Kenji Shimizu, Sachiko Miyamoto, Kazushi Aoto, Mitsuko Nakashima, Tomomi Yamaguchi, Tomoki Kosho, Tsutomu Ogata, Hirotomo Saitsu
Topics & Concepts
ProbandBiologyGeneticsExome sequencingExonIntronDNA sequencingGeneGenomeRNA splicingRNAPhenotypeMutationConnective tissue disorders researchGenomics and Rare DiseasesProtease and Inhibitor Mechanisms