CRISPR/cas genome editing for neurodegenerative diseases: Mechanisms, therapeutic advances, and clinical prospects
Kalpana Pandya, Devendra Kumar
Topics & Concepts
Genome editingGermlineBiologyDiseaseAmyotrophic lateral sclerosisZinc finger nucleaseSomatic cellGenomeComputational biologymicroRNATranscriptomeGeneticsPrecision medicineRNA editingAtaxiaBioinformaticsGeneDisease gene identificationCRISPRMedicineLRRK2GenomicsGermline mutationNeuroscienceMutationExomeGenetic disorderCRISPR and Genetic EngineeringInnovation and Socioeconomic DevelopmentGenetics, Aging, and Longevity in Model Organisms