Current and future treatments for sickle cell disease: From hematopoietic stem cell transplantation to in vivo gene therapy
Julia Ball, Avery Bradley, Anh‐Tuan Le, John F. Tisdale, Naoya Uchida
Topics & Concepts
Genetic enhancementHematopoietic stem cell transplantationTransplantationStem cellIn vivoDiseaseHaematopoiesisBiologyHematopoietic stem cellCancer researchGeneImmunologyMedicineGeneticsInternal medicineHemoglobinopathies and Related DisordersVirus-based gene therapy researchNeurogenetic and Muscular Disorders Research