Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls
Suzanne Kroes, Marlou C. Bierlaagh, Juliet Lefferts, Alessandra Boni, Danya Muilwijk, C. Viscomi, Natascha D A Keijzer-Nieuwenhuijze, Luca Cristiani, Paul J Niemöller, Tibo F. Verburg, Renato Cutrera, Alessandro Fiocchi, V. Lucidi, Cornelis K. van der Ent, Jeffrey M. Beekman, Federico Alghisi, Fabiana Ciciriello
Topics & Concepts
IvacaftorCystic fibrosisMedicineOrganoidCystic fibrosis transmembrane conductance regulatorMutationBioinformaticsGeneticsInternal medicineBiologyGeneCystic Fibrosis Research AdvancesEnergy Harvesting in Wireless NetworksNeonatal Respiratory Health Research