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A comprehensive testing algorithm for the diagnosis of Fabry disease in males and females

Ashlee R. Stiles, Haoyue Zhang, Jian Dai, Patricia McCaw, James Beasley, Catherine Rehder, Dwight D. Koeberl, Marie McDonald, Deeksha Bali, Sarah P. Young

2020Molecular Genetics and Metabolism43 citationsDOI

Topics & Concepts

Fabry diseaseGlobotriaosylceramideBiomarkerInternal medicineSanger sequencingMedicineDiseaseAlpha-galactosidaseEnzyme replacement therapyGastroenterologyBiologyGeneDNA sequencingGeneticsLysosomal Storage Disorders ResearchTrypanosoma species research and implicationsGlycogen Storage Diseases and Myoclonus
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