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Assessment of a Clinical Trial Metric for Rett Syndrome: Critical Analysis of the Rett Syndrome Behavioural Questionnaire

Wei Hou, Usree Bhattacharya, Wisnu A. Pradana, Daniel Tarquinio

2020Pediatric Neurology31 citationsDOI

Topics & Concepts

Rett syndromeIntraclass correlationPhysical therapyMedicineClinical trialPsychologyKappaMECP2PediatricsClinical psychologyPsychometricsInternal medicineLinguisticsGeneBiochemistryPhilosophyPhenotypeChemistryGenetics and Neurodevelopmental DisordersFamily and Disability Support ResearchChild Nutrition and Feeding Issues
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