Litcius/Paper detail

Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts

Michael Stirm, Lina Marie Fonteyne, Bachuki Shashikadze, Jan B. Stöckl, Mayuko Kurome, Barbara Keßler, Valeri Zakhartchenko, Elisabeth Kemter, Helmut Blum, Georg J. Arnold, Kaspar Matiasek, Rüdiger Wanke, Wolfgang Wurst, Hiroshi Nagashima, Ferdinand Knieling, Maggie C. Walter, Christian Kupatt, Thomas Fröhlich, Nikolai Klymiuk, Andreas Blutke, Eckhard Wolf

2022Neuromuscular Disorders26 citationsDOIOpen Access PDF

Topics & Concepts

Duchenne muscular dystrophyDystrophinGenome editingCRISPRMedicineDiseaseExon skippingBioinformaticsMuscular dystrophySomatic cellPathologyBiologyExonGeneGeneticsInternal medicineAlternative splicingMuscle Physiology and DisordersTissue Engineering and Regenerative MedicineVirus-based gene therapy research