Real-Life Outcome After Gene Replacement Therapy for Spinal Muscular Atrophy: A Multicenter Experience
Itay Tokatly Latzer, Liora Sagi, Revital Lavi, Sharon Aharoni, Jacob Bistritzer, Iris Noyman, Mira Ginsburg, Angela Lev-Or, Sharona Katzenellenbogen, Yoram Nevo, Aviva Fattal‐Valevski
Topics & Concepts
MedicineSMA*Interquartile rangeSpinal muscular atrophyInternal medicineNeuromuscular diseaseDiseasePhysical therapyPediatricsCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchCardiomyopathy and Myosin StudiesHereditary Neurological Disorders