Efficacy and safety of azithromycin maintenance therapy in primary ciliary dyskinesia (BESTCILIA): a multicentre, double-blind, randomised, placebo-controlled phase 3 trial
Helene Kobbernagel, Frederik Buchvald, Eric G. Haarman, Carmen Casaulta, Samuel A. Collins, Claire Hogg, Claudia E. Kuehni, Jane S. Lucas, Claus Moser, Alexandra L. Quittner, Johanna Raidt, Susanne Rosthøj, Anne L. Sørensen, Kim Thomsen, Claudius Werner, Heymut Omran, Kim G. Nielsen
Topics & Concepts
MedicineAzithromycinPrimary ciliary dyskinesiaClinical endpointPlaceboClinical trialInternal medicinePediatricsRandomized controlled trialPhysical therapyBronchiectasisAntibioticsAlternative medicinePathologyLungMicrobiologyBiologyCystic Fibrosis Research AdvancesSinusitis and nasal conditionsRespiratory and Cough-Related Research