‘Channeling’ therapeutic discovery for epileptic encephalopathy through iPSC technologies
Dina Simkin, Christina M. Ambrosi, Kelly A. Marshall, Luis A. Williams, Jordyn Eisenberg, Mennat Gharib, Graham T. Dempsey, Alfred L. George, Owen B. McManus, Evangelos Kiskinis
Topics & Concepts
ChannelopathyInduced pluripotent stem cellEpilepsyNeuroscienceDiseaseMedicineGenome editingBioinformaticsBiologyGeneCRISPREmbryonic stem cellGeneticsPathologyCRISPR and Genetic EngineeringPluripotent Stem Cells ResearchNeuroscience and Neural Engineering