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The Bespoke Gene Therapy Consortium: facilitating development of AAV gene therapies for rare diseases

Philip J. Brooks, Timothy M. Miller, Frédéric Revah, Junghae Suh, Bradley R. Garrison, Lawrence C. Starke, Timothy K. MacLachlan, Edward Neilan, Gopa Raychaudhuri, Sadik H. Kassim, Jean Dehdashti, Joni L. Rutter

2024Nature Reviews Drug Discovery20 citationsDOI

Topics & Concepts

BespokeGeneral partnershipGenetic enhancementBusinessPublic–private partnershipMedicineGeneBiologyGeneticsFinanceAdvertisingCRISPR and Genetic EngineeringVirus-based gene therapy researchCAR-T cell therapy research
The Bespoke Gene Therapy Consortium: facilitating development of AAV gene therapies for rare diseases | Litcius