Design and analysis features used in small population and rare disease trials: A targeted review
Giles Partington, Suzie Cro, Alexina J. Mason, Rachel Phillips, Victoria Cornelius
Topics & Concepts
Frequentist inferenceSample size determinationPrior probabilityBayesian probabilityClinical trialPopulationMedicineMeta-analysisRandomized controlled trialStatisticsBayesian inferenceMathematicsInternal medicineEnvironmental healthStatistical Methods in Clinical TrialsGenetic Associations and EpidemiologyMeta-analysis and systematic reviews