Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus
David Moreno-Martínez, Patrício Aguiar, Christiane Auray‐Blais, Michael Beck, Daniel G. Bichet, Alessandro P. Burlina, David E. C. Cole, Perry Elliott, Ulla Feldt‐Rasmussen, Sandro Feriozzi, Janice M. Fletcher, Roberto Giugliani, Ana Jovanović, C. Kampmann, Mirjam Langeveld, Olivier Lidove, Aleš Linhart, Michael Mauer, James Moon, Alison Muir, Albina Nowak, João Paulo Oliveira, Alberto Ortíz, Guillem Pintos‐Morell, Juan Politei, Paula Rozenfeld, Raphael Schiffmann, Einar Svarstad, Andrew Talbot, Mark Thomas, Camilla Tøndel, David G. Warnock, Michael L. West, Derralynn Hughes
Topics & Concepts
DelphiFabry diseaseDelphi methodClinical trialMedicineDiseaseInternal medicineComputer scienceArtificial intelligenceOperating systemLysosomal Storage Disorders ResearchWhipple's Disease and InterleukinsParasitic Diseases Research and Treatment