Litcius/Paper detail

CRISPR-Cas9-Mediated ELANE Mutation Correction in Hematopoietic Stem and Progenitor Cells to Treat Severe Congenital Neutropenia

Ngoc Tung Tran, Robin Graf, Annika Wulf-Goldenberg, Maria Stecklum, Gabriele Strauß, Ralf Kühn, Christine Kocks, Klaus Rajewsky, Van Trung Chu

2020Molecular Therapy47 citationsDOIOpen Access PDF

Topics & Concepts

Congenital NeutropeniaBiologyProgenitor cellHaematopoiesisCancer researchStem cellMutationImmunologyGeneticsGeneBlood disorders and treatmentsImmunodeficiency and Autoimmune DisordersErythrocyte Function and Pathophysiology
CRISPR-Cas9-Mediated ELANE Mutation Correction in Hematopoietic Stem and Progenitor Cells to Treat Severe Congenital Neutropenia | Litcius